Neuropediatrics 2018; 49(S 02): S1-S69
DOI: 10.1055/s-0038-1676033
DOI: 10.1055/s-0038-1676033
Industrial Posters
Therapy Strategies and Free Topics
IP 853. AVXS-101 Phase-1-Gene Therapy Clinical Trial in SMA Type 1: Event-Free Survival and Achievement of Developmental Milestones
Authors
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Jerry R. Mendell
1 Center for Gene Therapy Nationwide Children’s Hospital, Columbus, United States2 Department of Pediatrics, Ohio State University, Columbus, United States3 Department of Neurology, Ohio State University, Columbus, United States -
Samiah Al-Zaidy
1 Center for Gene Therapy Nationwide Children’s Hospital, Columbus, United States2 Department of Pediatrics, Ohio State University, Columbus, United States -
Richard Shell
4 Section of Pulmonary Medicine, Department of Pediatrics, Nationwide Children’s Hospital, Columbus, United States5 Section of Pulmonary Medicine, Department of Pediatrics, Ohio State University, Columbus, United States -
W. Dave Arnold
3 Department of Neurology, Ohio State University, Columbus, United States -
Louise Rodino-Klapac
1 Center for Gene Therapy Nationwide Children’s Hospital, Columbus, United States3 Department of Neurology, Ohio State University, Columbus, United States -
Thomas W. Prior
6 Department of Pathology, Ohio State University, Columbus, United States -
Linda P. Lowes
1 Center for Gene Therapy Nationwide Children’s Hospital, Columbus, United States3 Department of Neurology, Ohio State University, Columbus, United States -
Lindsay N. Alfano
1 Center for Gene Therapy Nationwide Children’s Hospital, Columbus, United States -
Katherine Berry
1 Center for Gene Therapy Nationwide Children’s Hospital, Columbus, United States -
Kathleen Church
1 Center for Gene Therapy Nationwide Children’s Hospital, Columbus, United States -
John T. Kissel
2 Department of Pediatrics, Ohio State University, Columbus, United States -
Sukumar Nagendran
7 AveXis, Inc., Bannockburn, United States -
James L’italien
7 AveXis, Inc., Bannockburn, United States -
Douglas M. Sproule
7 AveXis, Inc., Bannockburn, United States -
Courtney Wells
7 AveXis, Inc., Bannockburn, United States -
Arthur H. M. Burghes
3 Department of Neurology, Ohio State University, Columbus, United States8 Department of Biological Chemistry and Pharmacology, Ohio State University, Columbus, United States -
Kevin D. Foust
7 AveXis, Inc., Bannockburn, United States -
Kathrin Meyer
1 Center for Gene Therapy Nationwide Children’s Hospital, Columbus, United States -
Shibi Likhite
1 Center for Gene Therapy Nationwide Children’s Hospital, Columbus, United States -
Brian K. Kaspar
1 Center for Gene Therapy Nationwide Children’s Hospital, Columbus, United States2 Department of Pediatrics, Ohio State University, Columbus, United States3 Department of Neurology, Ohio State University, Columbus, United States7 AveXis, Inc., Bannockburn, United States
