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Neuropediatrics 2019; 50(S 02): S1-S55
DOI: 10.1055/s-0039-1698255
Poster Presentations
Poster Area GNP Neuromuscular Diseases/Varia 2
Georg Thieme Verlag KG Stuttgart · New York

Effect of Ataluren on Age at Loss of Ambulation in Nonsense Mutation Duchenne Muscular Dystrophy: Observational Data from the STRIDE Registry

Christian Werner
1   PTC Therapeutics Germany GmbH, Frankfurt, Germany
,
Abdallah Delage
2   PTC Therapeutics, Global Medical Affairs, Zug, Switzerland
,
Filippo Buccella
3   Duchenne Parent Project Italy, Duchenne Parent Project, Rome, Italy
,
Isabelle Desguerre
4   Necker – Enfants Malades Hospital, Paris V Descartes University, Neuromuscular Network FILNEMUS, Paris, France
,
Francesco Muntoni
5   University College London & Great Ormond Street Hospital Trust, NIHR Great Ormond Street Hospital Biomedical Research Centre, Great Ormond Street Institute of Child Health, London, United Kingdom
,
Andrés Nascimento
6   Hospital Sant Joan de Déu, Universidad de Barcelona, Unidad de Patología Neuromuscular, Barcelona, Spain
,
Már Tulinius
7   Gothenburg University, Queen Silvia Children’s Hospital, Gothenburg, Sweden
,
Allan Kristensen
8   PTC Therapeutics, Inc., Biostatistics, South Plainfield, NJ, United States
,
Claudio Santos
9   PTC Therapeutics, Inc., Global Medical Affairs, South Plainfield, NJ, United States
,
Panayiota Trifillis
9   PTC Therapeutics, Inc., Global Medical Affairs, South Plainfield, NJ, United States
,
Olivia Zhang
8   PTC Therapeutics, Inc., Biostatistics, South Plainfield, NJ, United States
,
Eugenio Mercuri
10   Catholic University, Department of Pediatric Neurology, Rome, Italy
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