Mirko Essing
8
Orchard Therapeutics (Europe) Limited
,
Alberto Zambon
3
Neurology Department, IRCCS San Raffaele Scientific Institute, Milan, Italy
9
Vita-Salute San Raffaele University, Milan, Italy
12
Department of Neurology, ASST Papa Giovanni XXIII; Bergamo, Italy
,
Vera Gallo
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Cristina Baldoli
4
Neuroradiology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Federica Cugnata
5
University Centre of Statistics in the Biomedical Sciences, Vita-Salute San Raffaele University, Milan, Italy
,
Paola M. V. Rancoita
5
University Centre of Statistics in the Biomedical Sciences, Vita-Salute San Raffaele University, Milan, Italy
,
Fabiola De Mattia
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Elena Fratini
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
9
Vita-Salute San Raffaele University, Milan, Italy
12
Department of Neurology, ASST Papa Giovanni XXIII; Bergamo, Italy
,
Salvatore Recupero
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
9
Vita-Salute San Raffaele University, Milan, Italy
12
Department of Neurology, ASST Papa Giovanni XXIII; Bergamo, Italy
,
Francesca Ferrua
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Federica Barzaghi
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Maria Pia Cicalese
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Maddalena Migliavacca
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Francesca Tucci
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Francesca Ciotti
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Maddalena Fraschini
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Marina Sarzana
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Stefano Scarparo
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Paolo Silvani
6
Department of Anesthesia and Critical Care, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Sara Locatelli
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Alessandra Clerici
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Gigliola Antonioli
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Mara Sangalli
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Stefano Zancan
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Andrea Calabria
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Eugenio Montini
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Giada Farinelli
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Francesco Morena
7
Department of Chemistry, Biology and Biotechnologies, University of Perugia, Perugia, Italy
,
Jesus Segovia
8
Orchard Therapeutics (Europe) Limited
,
Laetitia C. Schwab
8
Orchard Therapeutics (Europe) Limited
,
Gerald Downey
8
Orchard Therapeutics (Europe) Limited
,
Michela Gabaldo
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Sabata Martino
7
Department of Chemistry, Biology and Biotechnologies, University of Perugia, Perugia, Italy
,
Clelia Di Serio
9
Vita-Salute San Raffaele University, Milan, Italy
,
Fabio Ciceri
9
Vita-Salute San Raffaele University, Milan, Italy
10
Unit of Hematology and Bone Marrow Transplantation, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Massimo Filippi
3
Neurology Department, IRCCS San Raffaele Scientific Institute, Milan, Italy
9
Vita-Salute San Raffaele University, Milan, Italy
11
Neuroimaging Research Unit, Institute of Experimental Neurology (INSPE), Division of Neuroscience, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Maria Sessa
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
12
Department of Neurology, ASST Papa Giovanni XXIII; Bergamo, Italy
,
Maria Grazia Natali Sora
3
Neurology Department, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Maria Ester Bernardo
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
,
Luigi Naldini
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
9
Vita-Salute San Raffaele University, Milan, Italy
,
Alessandra Biffi
13
Pediatric Hematology, Oncology and Stem Cell Transplant, Padua University and Hospital, Padua, Italy
14
Gene Therapy Program, Dana Farber/Boston Children's Cancer and Blood Disorders Center, Boston, Massachusetts, United States
,
Alessandro Aiuti
1
San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), IRCCS San Raffaele Scientific Institute, Milan, Italy
2
Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
9
Vita-Salute San Raffaele University, Milan, Italy
› Author Affiliations